Stanford researchers have developed a highly specific, tunable system to improve the safety, efficacy and deliverability of gene therapy vectors and other biological therapies.
Researchers in Dr. Mark Kay's laboratory at Stanford University have designed a new liver-specific expression cassette for inserting genes into double-stranded AAV (adeno-associated virus) vectors for gene therapy.
Researchers at Stanford have developed and patented rAAV vectors that can be used to transfer long nucleic acids into cells. Recombinant AAV vectors are limited by a restricted amount of exogenous DNA that can be placed into the vector.